Gene therapy improves hearing in 90% of patients with inherited deafness in largest trial of its kind

livescience - A new gene therapy tested in China has improved the hearing of 38 people who were born deaf due to mutations in a gene called OTOF.

AI Summary: A gene therapy for inherited deafness delivered dramatic results, restoring hearing in roughly 90% of treated patients in the largest trial of its kind. Investigators report durable improvements over follow-up, signaling a potential one-time intervention for certain genetic deafness types and challenging the notion that auditory loss is always irreversible. Hope, meet hard data.

• FDA approves first-ever gene therapy for inherited hearing loss (6)
• Primate study finds human-like genetic cause of blindness (1)
• Trial shows durable hearing restored in most patients (3)

FDA approves first-ever gene therapy for inherited hearing loss

Primate study finds human-like genetic cause of blindness

Trial shows durable hearing restored in most patients